Publications

Title page of a scientific research paper titled 'Symmetric Age-association of Retinal Degeneration in Patients with CLN2-Associated Batten Disease' from HHS Public Access, authored by Kyle D Kovacs and colleagues, published in 'Ophthalmol Retina' in 2020.
First page of a scientific article titled 'Characterization of AAV-mediated dorsal root ganglionopathy' from Molecular Therapy journal, showing the article's abstract and publication details.
Research article from Cell Reports Medicine about recreating CLN2 disease pathology using hiPSC-derived retinal organoids and retina-on-chip systems, including diagrams of healthy and diseased retinal cells and gene therapy correction.
Journal article titled 'Gene therapy ameliorates spontaneous seizures associated with cortical neuron loss in a Cln2R207X mouse model' with author list and abstract visible.
Scientific research paper titled 'OCT Biomarkers in Ocular CLN2 Disease in Patients Treated with Intravitreal Enzyme Replacement Therapy' with authors and affiliations, discussing optical coherence tomography analyses of retinal parameters and related disease progression.
SAVING VISION  |  IMPROVING LIVES